An Observational, Longitudinal, Prospective, Long-Term Registry of Patients with hypophosphatasia ClinicalTrials.gov ID NCT02306720 Sponsor Alexion Pharmaceuticals, Inc. Information provided by Alexion Pharmaceuticals, Inc. (Responsible Party) Last Update Posted 2024-09-19 Study Overview In this...
A Non-Interventional Post-Authorization Safety Study (PASS) of Carbaglu® for the Treatment ofHyperammonemia Due to Methylmalonic Acidemia (MMA) and Propionic Acidemia (PA)in Adult and Pediatric Patient Populations ClinicalTrials.gov ID NCT05040178 Sponsor Recordati Rare Diseases Information provided...
A Phase 1, First-In-Human, Multiple Part, Single Ascending and Multiple Dose Study of JNT-517 in Healthy Participants and in Participants with Phenylketonuria ClinicalTrials.gov ID NCT05781399 Sponsor Jnana Therapeutics Information provided by Jnana Therapeutics (Responsible Party) Last Update...
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The rich text element allows you to create and format headings, paragraphs, blockquotes, images, and video all in one place instead of having to add and format them individually. Just double-click and easily create content. Static and dynamic content editing A rich text element can be used with...